Target That Could Ease Spinal Muscular Atrophy Symptoms Discovered
Wednesday, January 7, 2009 - 13:15
in Health & Medicine
There is no cure for spinal muscular atrophy (SMA), a genetic disorder that causes the weakening of muscles and is the leading genetic cause of infant death, but researchers have discovered a new therapeutic target that improves deteriorating skeletal muscle tissue caused by SMA. The new therapy enhanced muscle strength, improved gross motor skills and increased the lifespan in a SMA model.