Clinical trial for muscular dystrophy demonstrates safety of customized gene therapy
Wednesday, November 30, 2011 - 23:30
in Health & Medicine
Researchers have shown that it is safe to cut and paste together different viruses in an effort to create the ultimate vehicle for gene therapy. In a phase I clinical trial, the investigators found no side effects from using a "chimeric" virus to deliver replacement genes for an essential muscle protein in patients with muscular dystrophy.