Prime editing repairs five genetic mutations to treat rare brain disorder in mice
Monday, July 21, 2025 - 11:13
in Health & Medicine
By the time they are a few months old, infants born with alternating hemiplegia of childhood (AHC) begin experiencing terrifying episodes of paralysis and seizures, and will soon show developmental delays and intellectual disability. There is no cure or effective treatment for this rare genetic disease, but new research suggests a potential path to one.