New molecule heralds hope for muscular dystrophy treatment
Tuesday, April 30, 2013 - 05:00
in Health & Medicine
(Phys.org) —There's hope for patients with myotonic dystrophy. A new small molecule developed by researchers at the University of Illinois has been shown to break up the protein-RNA clusters that cause the disease in living human cells, an important first step toward developing a pharmaceutical treatment for the as-yet untreatable disease.