Scientists use nanoparticle-delivered gene therapy to inhibit blinding eye disease in rodents
Tuesday, July 7, 2020 - 11:40
in Biology & Nature
In experiments in rats and mice, two Johns Hopkins scientists—an engineer and an ophthalmologist—report the successful use of nanoparticles to deliver gene therapy for blinding eye disease. A uniquely engineered large molecule allows researchers to compact large bundles of therapeutic DNA to be delivered into the cells of the eye.